Search for Clinical Trial Results
Peroxisomal Biogenesis Disorders - 25 Studies Found
Status | Study |
Active, not recruiting |
Study Name: MD1003-AMN MD1003 in Adrenomyeloneuropathy Condition:
Date: 2016-11-09 Interventions:
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Recruiting |
Study Name: Newborn Screening for Adrenoleukodystrophy Condition: Adrenoleukodystrophy Date: 2016-10-31 Interventions: Procedure: newborns testing for ALD Routine newborn screening dried blood spots sample is used to test i |
Not yet recruiting |
Study Name: Early Diagnosis Of Childhood Cerebral ALD Condition: Adrenoleukodystrophy Date: 2016-10-25 |
Enrolling by invitation |
Study Name: Long-term Follow-up of Subjects With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug Product Condition:
Date: 2015-08-12 Interventions: Genetic: transduced CD34+ hematopoietic stem cell Autologous hematopoietic stem cells (HSCs) collected f |
Recruiting |
Study Name: Inherited Retinal Degenerative Disease Registry Condition:
Date: 2015-04-03 |
Withdrawn |
Study Name: MT2014-14 IT-MSC for Advanced Cerebral Adrenoleukodystrophy (cALD) Condition: Cerebral Adrenoleukodystrophy Date: 2015-03-27 Interventions: Biological: Mesenchymal Stem Cells |
Recruiting |
Study Name: UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells Condition:
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Available |
Study Name: Expanded Access for Lorenzo's Oil (GTO/GTE) in Adrenoleukodystrophy Condition: X-linked Adrenoleukodystrophy Date: 2014-05-05 Interventions: Drug: Lorenzo's Oil Oral use of Lorenzo's oil to lower very long chain fatty acids |